Prognostic factors for pulmonary milestones in Duchenne muscular dystrophy
Prognostic factors for pulmonary milestones in Duchenne muscular dystrophy
Knowledge of prognostic factors for pulmonary outcomes in DMD serves a general understanding of natural history and can help facilitate externally controlled studies and the long-term evaluation of novel therapies. This study assessed prognostic factors for time to forced vital capacity (FVC) %-predicted < 80% and time to FVC %-predicted < 50% using Cox proportional hazards analyses.
This poster was presented at WMS 2021.
Authors: N. Goemans, J. Signorovitch, G. Sajeev, B. Wong, C. Tian, C. McDonald, E. Mercuri, E. Niks, J. Freimark, M. Jenkins, C. Xu, and S. Ward.