Real-world and natural history data for drug evaluation in Duchenne muscular dystrophy: suitability of the North Star Ambulatory Assessment for comparisons with external controls Poster: A Concisely Recorded Ambulatory Assessment for Enhancing Real-World Outcomes Research in Duchenne Muscular Dystrophy: Development and Validation Poster: Predicting Trajectories of Ambulatory Function in Duchenne Muscular Dystrophy Predicting Trajectories of Ambulatory Function in Duchenne Muscular Dystrophy View the PDF
