Nature Biotechnology: Their Lives in Their Hands
cTAP has been included in an article featured in Nature Biotechnology: Their Lives in Their Hands. View the Full PDF
cTAP Publishes Comprehensive Analysis of NSAA
The collaborative Trajectory Analysis Project (cTAP), a multi-stakeholder, global coalition in Duchenne muscular dystrophy (DMD), has published research in the journal PLOS ONE providing quantitative insights to assist the design and analysis of clinical trials in patients with DMD. READ FULL PRESS RELEASE ON BUSINESSWIRE: cTAP Publishes Comprehensive Analysis of the North Star Ambulatory Assessment (NSAA), a Newly Adopted Primary Outcome Measure in Clinical Trials of Patients with Duchenne Muscular Dystrophy
Categorising trajectories and individual item changes of the NSAA in patients with DMD
Categorising trajectories and individual item changes of the North Star Ambulatory Assessment in patients with Duchenne muscular dystrophy Francesco Muntoni, Joana Domingos, Adnan Y. Manzur, Anna Mayhew, Michela Guglieri, The UK NorthStar Network, Gautam Sajeev, James Signorovitch, Susan J. Ward. PLoS One. 2019 Sep 3;14(9):e0221097. doi: 10.1371/journal.pone.0221097. eCollection 2019 View the Full PDF
2019 EAN Abstract – Phase 1b/2 Study of RG6206
A Phase 1b/2 study of the anti-myostatin adnectin RG6206 (BMS-986089) in ambulatory boys with Duchenne muscular dystrophy: A 72-week treatment update View the Full PDF
cTAP Abstract for 2019 NORD Summit
August 2019 cTAP abstract entitled "Pioneering collaborative analytics to accelerate therapy approval and access in rare disease" for the 2019 NORD Summit. View the Full PDF
2019 EU ISPOR Abstract – NSAA consistency analysis
SUITABILITY OF NATURAL HISTORY DATA FOR EXTERNAL CONTROLS IN DUCHENNE MUSCULAR DYSTROPHY View the Full PDF
2019 EU ISPOR Abstract – Prognostic Model for Loss of Walking in DMD
A COMPOSITE PROGNOSTIC SCORE FOR TIME TO LOSS OF WALKING ABILITY IN DUCHENNE MUSCULAR DYSTROPHY (DMD) View the Full PDF
2019 JSCN Abstract – Phase 1b/2 Study of RG6206
A Phase 1b/2 study of RG6206 (BMS-986089) in boys with Duchenne muscular dystrophy: 72-week update View the Full PDF
2019 MDA Abstract – NSAA Shift Analyses
One-year shifts in North Star Ambulatory Assessment items in Duchene muscular dystrophy (DMD) patients in the UK NorthStar Network database View the Full PDF
2019 MDA Abstract – The Collaborative Trajectory Analysis Project (cTAP)
The collaborative Trajectory Analysis Project (cTAP) – pioneering collaborative analytics for more effective clinical trials in Duchenne Muscular Dystrophy View the Full PDF